Low Evidence Drugs

Exploratory candidates requiring substantial validation


Evidence Standards

Level Definition Clinical Significance
L4 Case reports or preclinical only Very limited evidence, exploratory research
L5 AI prediction only, no clinical evidence Hypothesis generation, needs validation

Drug List

L4 Level (0 drugs)

| Drug Name | Predictions | Link | |———–|————-|——|

L4 drug reports are being prepared.

L5 Level (508 drugs)

Drug Name Predictions Link
Acalabrutinib 3 View Report
Acarbose 10 View Report
Aceclofenac 7 View Report
Acetaminophen 7 View Report
Acetazolamide 18 View Report
Acetic Acid 2 View Report
Acetylcysteine 232 View Report
Acetylsalicylic Acid 26 View Report
Acyclovir 252 View Report
Adalimumab 180 View Report
Adapalene 5 View Report
Adenosine 2 View Report
Aflibercept 20 View Report
Agomelatine 4 View Report
Albendazole 72 View Report
Albutrepenonacog Alfa 8 View Report
Alemtuzumab 1 View Report
Alfacalcidol 56 View Report
Alfuzosin 1 View Report
Allopurinol 33 View Report
Alprazolam 42 View Report
Alprostadil 18 View Report
Ambrisentan 2 View Report
Ammonium Chloride 99 View Report
Amoxicillin 24 View Report
Amphotericin B 106 View Report
Ampicillin 35 View Report
Anidulafungin 2 View Report
Apalutamide 3 View Report
Apremilast 3 View Report
Aripiprazole 150 View Report
Arsenic Trioxide 3 View Report
Artesunate 3 View Report
Ascorbic Acid 36 View Report
Asfotase Alfa 2 View Report
Aspartic Acid 21 View Report
Atenolol 180 View Report
Atezolizumab 2 View Report
Atovaquone 3 View Report
Avanafil 9 View Report
Avelumab 1 View Report
Axitinib 8 View Report
Azacitidine 204 View Report
Azathioprine 3 View Report
Azelaic Acid 4 View Report
Azithromycin 48 View Report
Bacitracin 3 View Report
Baloxavir Marboxil 2 View Report
Baricitinib 2 View Report
Beclomethasone Dipropionate 147 View Report
Belimumab 2 View Report
Benralizumab 2 View Report
Benzbromarone 2 View Report
Benzocaine 30 View Report
Benzoic Acid 80 View Report
Benzoyl Peroxide 54 View Report
Beractant 4 View Report
Betamethasone 3198 View Report
Bevacizumab 180 View Report
Bezafibrate 2 View Report
Bilastine 20 View Report
Bimatoprost 12 View Report
Biotin 2 View Report
Bisacodyl 13 View Report
Bortezomib 64 View Report
Brentuximab Vedotin 5 View Report
Brexpiprazole 30 View Report
Brigatinib 6 View Report
Brinzolamide 6 View Report
Brolucizumab 1 View Report
Budesonide 216 View Report
Bumetanide 3 View Report
Bupropion 10 View Report
Burosumab 3 View Report
Cabergoline 4 View Report
Cabozantinib 15 View Report
Caffeine 108 View Report
Calcifediol 7 View Report
Calcitriol 42 View Report
Calcium Carbonate 96 View Report
Calcium Chloride 80 View Report
Calcium Lactate 18 View Report
Calcium Lactate Gluconate 3 View Report
Candesartan Cilexetil 26 View Report
Capecitabine 72 View Report
Capsaicin 4 View Report
Captopril 18 View Report
Carbamazepine 96 View Report
Carbetocin 4 View Report
Carbidopa 90 View Report
Carbimazole 12 View Report
Carboplatin 42 View Report
Carfilzomib 2 View Report
Carvedilol 28 View Report
Cefaclor 10 View Report
Cefixime 40 View Report
Cefotaxime 11 View Report
Ceftazidime 105 View Report
Ceftriaxone 27 View Report
Celecoxib 198 View Report
Cephalexin 64 View Report
Ceritinib 2 View Report
Cetuximab 7 View Report
Chlorambucil 9 View Report
Chloramphenicol 140 View Report
Chlordiazepoxide 9 View Report
Chlorthalidone 9 View Report
Cholecalciferol 50 View Report
Ciclesonide 25 View Report
Cilostazol 3 View Report
Cimetidine 252 View Report
Cinchocaine 1 View Report
Cinnarizine 10 View Report
Ciprofloxacin 280 View Report
Cisplatin 42 View Report
Citalopram 6 View Report
Citric Acid 18 View Report
Cladribine 6 View Report
Clarithromycin 252 View Report
Clavulanic Acid 110 View Report
Clobazam 2 View Report
Clobetasol Propionate 224 View Report
Clofarabine 4 View Report
Clofazimine 12 View Report
Clonazepam 24 View Report
Clopidogrel 3 View Report
Clotrimazole 549 View Report
Colchicine 21 View Report
Crisaborole 2 View Report
Crizotinib 4 View Report
Crotamiton 27 View Report
Cyanocobalamin 320 View Report
Cyclophosphamide 14 View Report
Cycloserine 1 View Report
Cyclosporine 4 View Report
Cytarabine 60 View Report
Dacarbazine 12 View Report
Danazol 9 View Report
Dapagliflozin 28 View Report
Dapsone 6 View Report
Daratumumab 2 View Report
Darunavir 2 View Report
Dasatinib 4 View Report
Decitabine 96 View Report
Deferasirox 98 View Report
Deferiprone 48 View Report
Delamanid 1 View Report
Denosumab 18 View Report
Desloratadine 230 View Report
Desmopressin 12 View Report
Desonide 25 View Report
Dexamethasone 2736 View Report
Dexlansoprazole 8 View Report
Dexpanthenol 30 View Report
Dextromethorphan 35 View Report
Diazepam 56 View Report
Digoxin 8 View Report
Dimenhydrinate 30 View Report
Dinoprostone 6 View Report
Docetaxel 70 View Report
Dolutegravir 2 View Report
Drospirenone 21 View Report
Dulaglutide 4 View Report
Dupilumab 4 View Report
Durvalumab 1 View Report
Dutasteride 14 View Report
Ebastine 6 View Report
Eculizumab 2 View Report
Edaravone 3 View Report
Efavirenz 22 View Report
Elosulfase Alfa 1 View Report
Elvitegravir 2 View Report
Emicizumab 4 View Report
Empagliflozin 30 View Report
Emtricitabine 24 View Report
Entacapone 88 View Report
Entecavir 1 View Report
Enzalutamide 12 View Report
Epinephrine 16 View Report
Eplerenone 4 View Report
Eptinezumab 2 View Report
Erenumab 4 View Report
Ergocalciferol 11 View Report
Erythromycin 88 View Report
Eslicarbazepine Acetate 8 View Report
Estradiol 24 View Report
Estradiol Valerate 3 View Report
Etanercept 35 View Report
Ethinylestradiol 105 View Report
Ethionamide 1 View Report
Etoposide 16 View Report
Everolimus 80 View Report
Evolocumab 4 View Report
Ezetimibe 234 View Report
Famotidine 135 View Report
Favipiravir 2 View Report
Febuxostat 11 View Report
Felodipine 10 View Report
Fenofibrate 78 View Report
Ferrous Fumarate 91 View Report
Ferrous Gluconate 5 View Report
Filgrastim 16 View Report
Finasteride 8 View Report
Fluconazole 182 View Report
Fluocinolone Acetonide 51 View Report
Fluorometholone 13 View Report
Fluorouracil 57 View Report
Flurbiprofen 12 View Report
Flutamide 3 View Report
Fluticasone Furoate 20 View Report
Fluticasone Propionate 540 View Report
Folic Acid 132 View Report
Furosemide 15 View Report
Fusidic Acid 3008 View Report
Gabapentin 38 View Report
Galcanezumab 4 View Report
Galsulfase 1 View Report
Ganciclovir 3 View Report
Gatifloxacin 10 View Report
Gefitinib 20 View Report
Gemfibrozil 8 View Report
Gilteritinib 15 View Report
Gimeracil 10 View Report
Gliclazide 72 View Report
Glimepiride 20 View Report
Glipizide 4 View Report
Glycine 192 View Report
Golimumab 12 View Report
Griseofulvin 42 View Report
Guaiacol 4 View Report
Guaifenesin 56 View Report
Haloperidol 18 View Report
Hydrochlorothiazide 165 View Report
Hydrocortisone 2780 View Report
Hydrocortisone Acetate 2880 View Report
Hydroxyurea 58 View Report
Ibrutinib 45 View Report
Ibuprofen 360 View Report
Idursulfase 1 View Report
Iloprost 1 View Report
Imidafenacin 1 View Report
Imiglucerase 1 View Report
Imipenem 16 View Report
Imiquimod 22 View Report
Indapamide 42 View Report
Indomethacin 45 View Report
Infliximab 40 View Report
Insulin Aspart 30 View Report
Insulin Degludec 10 View Report
Insulin Detemir 6 View Report
Insulin Glargine 65 View Report
Insulin Glulisine 2 View Report
Insulin Human 110 View Report
Insulin Lispro 15 View Report
Ipilimumab 1 View Report
Irbesartan 141 View Report
Iron 90 View Report
Isoniazid 5 View Report
Isotretinoin 16 View Report
Itraconazole 55 View Report
Ixekizumab 4 View Report
Ketoconazole 759 View Report
Ketoprofen 40 View Report
Lactulose 36 View Report
Lamivudine 90 View Report
Lamotrigine 100 View Report
Lansoprazole 27 View Report
Laronidase 4 View Report
Latanoprost 34 View Report
Ledipasvir 2 View Report
Leflunomide 10 View Report
Lemborexant 2 View Report
Lenalidomide 100 View Report
Lercanidipine 2 View Report
Letermovir 2 View Report
Levetiracetam 44 View Report
Levodopa 150 View Report
Levofloxacin 52 View Report
Levonorgestrel 24 View Report
Levosimendan 2 View Report
Lidocaine 108 View Report
Linagliptin 18 View Report
Linezolid 45 View Report
Liraglutide 6 View Report
Lisinopril 36 View Report
Lithium Carbonate 11 View Report
Lixisenatide 4 View Report
Lonoctocog Alfa 10 View Report
Loperamide 2 View Report
Lopinavir 14 View Report
Loratadine 297 View Report
Lorazepam 40 View Report
Lorlatinib 4 View Report
Loteprednol Etabonate 26 View Report
Lovastatin 32 View Report
Lumefantrine 8 View Report
Luspatercept 14 View Report
Macitentan 1 View Report
Magnesium Carbonate 48 View Report
Magnesium Hydroxide 162 View Report
Magnesium Oxide 14 View Report
Magnesium Sulfate 24 View Report
Magnesium Trisilicate 65 View Report
Mannitol 18 View Report
Mebendazole 33 View Report
Medroxyprogesterone Acetate 63 View Report
Megestrol Acetate 12 View Report
Meloxicam 119 View Report
Melphalan 44 View Report
Mepolizumab 4 View Report
Mercaptopurine 5 View Report
Mesalazine 48 View Report
Methimazole 3 View Report
Methotrexate 150 View Report
Methyldopa 6 View Report
Methylene Blue 2 View Report
Methylphenidate 35 View Report
Methylprednisolone 118 View Report
Methylprednisolone Hemisuccinate 3 View Report
Metronidazole 425 View Report
Miconazole 8 View Report
Midazolam 6 View Report
Midostaurin 42 View Report
Minoxidil 45 View Report
Mirabegron 2 View Report
Mirtazapine 32 View Report
Moclobemide 3 View Report
Mometasone Furoate 640 View Report
Moroctocog Alfa 8 View Report
Moxifloxacin 16 View Report
Moxonidine 9 View Report
Mupirocin 20 View Report
Naltrexone 3 View Report
Naproxen 100 View Report
Netarsudil 4 View Report
Nevirapine 6 View Report
Nicotinamide 42 View Report
Nicotine 12 View Report
Nifedipine 27 View Report
Nimodipine 4 View Report
Nitrazepam 2 View Report
Nitric Oxide 3 View Report
Nivolumab 4 View Report
Norethisterone 40 View Report
Norfloxacin 150 View Report
Nystatin 12 View Report
Obinutuzumab 2 View Report
Ocrelizumab 1 View Report
Octreotide 12 View Report
Ofatumumab 2 View Report
Ofloxacin 690 View Report
Olanzapine 224 View Report
Olaparib 54 View Report
Omalizumab 28 View Report
Omeprazole 126 View Report
Omidenepag Isopropyl 4 View Report
Orlistat 4 View Report
Oxaliplatin 9 View Report
Oxcarbazepine 4 View Report
Oxytocin 4 View Report
Paclitaxel 370 View Report
Paliperidone 30 View Report
Palivizumab 1 View Report
Panitumumab 1 View Report
Pantoprazole 16 View Report
Pantothenic Acid 2 View Report
Pegaspargase 4 View Report
Pembrolizumab 3 View Report
Pentoxifylline 6 View Report
Perampanel 6 View Report
Perindopril 16 View Report
Permethrin 12 View Report
Perphenazine 2 View Report
Pertuzumab 3 View Report
Phenol 4 View Report
Phentermine 6 View Report
Pimecrolimus 2 View Report
Pirfenidone 9 View Report
Piribedil 2 View Report
Piroxicam 32 View Report
Plerixafor 4 View Report
Polyethylene Glycol 3 View Report
Pomalidomide 12 View Report
Posaconazole 36 View Report
Potassium Acetate 6 View Report
Potassium Bicarbonate 24 View Report
Potassium Chloride 108 View Report
Potassium Citrate 27 View Report
Potassium Iodide 15 View Report
Prednisolone 3650 View Report
Prednisolone Acetate 20 View Report
Pregabalin 252 View Report
Prilocaine 4 View Report
Probenecid 2 View Report
Procaine Benzylpenicillin 30 View Report
Progesterone 63 View Report
Promethazine 7 View Report
Propylene Glycol 2 View Report
Propylthiouracil 4 View Report
Pyrazinamide 12 View Report
Racecadotril 5 View Report
Ramipril 48 View Report
Ramucirumab 20 View Report
Ranibizumab 7 View Report
Ranitidine 9 View Report
Ravulizumab 1 View Report
Rebamipide 4 View Report
Repaglinide 4 View Report
Resorcinol 6 View Report
Revefenacin 2 View Report
Riboflavin 2 View Report
Rifampicin 6 View Report
Rilpivirine 2 View Report
Riluzole 1 View Report
Rimegepant 2 View Report
Riociguat 10 View Report
Risankizumab 8 View Report
Risperidone 150 View Report
Ritonavir 48 View Report
Rituximab 90 View Report
Rivastigmine 25 View Report
Romiplostim 3 View Report
Romosozumab 2 View Report
Ropeginterferon Alfa-2B 3 View Report
Rufinamide 2 View Report
Salbutamol 14 View Report
Salicylic Acid 567 View Report
Selenium Sulfide 4 View Report
Selexipag 8 View Report
Selumetinib 2 View Report
Semaglutide 30 View Report
Serine 54 View Report
Silodosin 1 View Report
Siltuximab 4 View Report
Simoctocog Alfa 8 View Report
Simvastatin 528 View Report
Sirolimus 5 View Report
Sitagliptin 12 View Report
Sodium Citrate 90 View Report
Sodium Fluoride 3 View Report
Sofosbuvir 12 View Report
Spironolactone 7 View Report
Sulfamethoxazole 27 View Report
Sulpiride 3 View Report
Sunitinib 5 View Report
Tacrolimus 26 View Report
Tadalafil 115 View Report
Tafamidis 4 View Report
Tafluprost 6 View Report
Tazobactam 10 View Report
Tegafur 15 View Report
Teicoplanin 1 View Report
Telmisartan 348 View Report
Temozolomide 15 View Report
Tenecteplase 8 View Report
Terbinafine 6 View Report
Teriflunomide 2 View Report
Teriparatide 10 View Report
Testosterone 90 View Report
Testosterone Undecanoate 4 View Report
Thalidomide 1 View Report
Theophylline 64 View Report
Thiotepa 117 View Report
Tibolone 2 View Report
Ticagrelor 32 View Report
Tigecycline 5 View Report
Timolol 4 View Report
Tiotropium 5 View Report
Tobramycin 78 View Report
Tocilizumab 14 View Report
Tolbutamide 2 View Report
Tolnaftate 112 View Report
Tolvaptan 18 View Report
Topiramate 48 View Report
Trabectedin 23 View Report
Tranexamic Acid 18 View Report
Trastuzumab 11 View Report
Trastuzumab Emtansine 2 View Report
Travoprost 8 View Report
Tretinoin 8 View Report
Triamcinolone 645 View Report
Triazolam 1 View Report
Trifarotene 1 View Report
Trifluridine 10 View Report
Trimethoprim 112 View Report
Tropicamide 1 View Report
Turoctocog Alfa 6 View Report
Turoctocog Alfa Pegol 8 View Report
Udenafil 6 View Report
Urea 18 View Report
Ursodeoxycholic Acid 15 View Report
Ustekinumab 24 View Report
Valproic Acid 6 View Report
Valsartan 82 View Report
Vedolizumab 8 View Report
Velpatasvir 4 View Report
Venetoclax 6 View Report
Vibegron 1 View Report
Vigabatrin 2 View Report
Vildagliptin 24 View Report
Voriconazole 50 View Report
Zanamivir 2 View Report
Zanubrutinib 3 View Report
Zidovudine 6 View Report
Zinc Gluconate 2 View Report
Zinc Oxide 504 View Report
Zoledronic Acid 20 View Report
Zopiclone 4 View Report

Understanding L4-L5 Evidence

L4: Case Reports & Preclinical

  • Individual case reports in literature
  • Animal model studies
  • In vitro experiments
  • Mechanism-based hypotheses

L5: AI Prediction Only

  • TxGNN model prediction without clinical validation
  • Based on knowledge graph relationships
  • High prediction score but no human studies
  • Starting point for research hypothesis

Value of L5 Predictions

While L5 represents the lowest evidence level, high-scoring L5 predictions can be valuable:

  1. Hypothesis Generation: Identify novel drug-disease relationships
  2. Research Prioritization: Focus resources on promising candidates
  3. Grant Applications: Support funding requests for validation studies
  4. Literature Mining: Guide systematic literature searches

Pathway to Higher Evidence

L4-L5 candidates can advance through:

Current Next Step Action Required
L5 L4 Publish case report or preclinical study
L4 L3 Complete Phase 1/2 trial or cohort study
L3 L2 Complete RCT or Phase 2 trial
L2 L1 Complete Phase 3 or systematic review

Disclaimer
L4-L5 evidence levels indicate very limited or no clinical validation. These predictions are for research hypothesis generation only. Do not use for clinical decisions without substantial further research.

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